Spinal Muscular Atrophy (SMA) Spinal muscular atrophy (SMA) is a genetic condition that causes worsening muscle weakness. There are five subtypes, which range in severity and age of …

Spinal Muscular Atrophy (SMA) is a neuromuscular disorder that causes early life mortality. Within the past decade, the Food and Drug Administration (FDA) has approved three novel …

There are several treatment options available for SMA. Learn more about drug therapies and supportive therapies here.

Feb 26, 2020 · Spinal muscular atrophy is a rare genetic condition that limits muscle development and causes weakness. Treatments are available, including targeted therapies that address the …

Jul 30, 2024 · Treatment early in life tends to provide more benefit than treatment later in life, as older people who have been living with SMA and have experienced greater loss of motor …

When determining a treatment plan with an adolescent or adult with SMA, consider factors such as quality of life, burden vs bene fit of treatment, and reproductive issues. Access to care co …

Multiple approaches are needed to preserve respiratory and muscle function, including physical therapy, nutritional support, and extensive medical equipment. Patients and caregivers …

There is currently no cure for spinal muscular atrophy (SMA), but there are treatments and support available to help people with SMA have the best possible quality of life. A range of …

Mar 24, 2025 · Here, BioSpace looks at six SMA therapies and novel formulations to watch in 2025 and beyond. Last week, Novartis announced positive safety and efficacy readouts for …

While 3 US Food and Drug Administration (FDA)-approved drugs are available for the treatment of spinal muscular atrophy (SMA), managing the disease requires a multidisciplinary team and …